The cost-effectiveness of enzyme replacement therapies versus best supportive care for treating late onset Pompe disease in the UK NHS

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Item Type:	Article
Authors/Creators:	Walton, Matthew James https://orcid.org/0000-0003-1932-3689 Deng, Jasmine (jasmine.deng@york.ac.uk) Corbett, Mark Stephen https://orcid.org/0000-0002-5937-1493 Umemneku-Chikere, Chinyereugo https://orcid.org/0000-0003-4114-2227 Nevitt, Sarah Jane https://orcid.org/0000-0001-9988-2709 Fulbright, Helen (helen.fulbright@york.ac.uk) Yew Tan, Chong Lachmann, Robin Churchill, Rachel https://orcid.org/0000-0002-1751-0512 Hodgson, Robert https://orcid.org/0000-0001-6962-2893
Copyright, Publisher and Additional Information:	© The Author(s) 2025
Dates:	Submitted: 29 March 2025 Accepted: 20 October 2025 Published (online): 18 November 2025
Institution:	The University of York
Academic Units:	The University of York > Faculty of Social Sciences (York) > Centre for Reviews and Dissemination (York)
Date Deposited:	23 Oct 2025 15:00
Last Modified:	19 Nov 2025 13:30
Published Version:	https://doi.org/10.1007/s10198-025-01868-2
Status:	Published online
Refereed:	Yes
Identification Number:	10.1007/s10198-025-01868-2
Open Archives Initiative ID (OAI ID):	oai:eprints.whiterose.ac.uk:233490

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Description: The cost-effectiveness of enzyme replacement therapies versus best supportive care for treating late onset Pompe disease in the UK NHS

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