Items where authors include "Mrug, M."

Article

Gansevoort, R.T., Hariri, A., Minini, P. et al. (11 more authors) (2023) Venglustat, a novel glucosylceramide synthase inhibitor, in patients at risk of rapidly progressing ADPKD: primary results of a double-blind, placebo-controlled, phase 2/3 randomized clinical trial. American Journal of Kidney Diseases, 81 (5). 517-527.e1. ISSN 0272-6386

Perrone, R.D., Hariri, A., Minini, P. et al. (10 more authors) (2022) The STAGED-PKD 2-stage adaptive study with a patient enrichment strategy and treatment effect modeling for improved study design efficiency in patients with ADPKD. Kidney Medicine, 4 (10). 100538. ISSN 2590-0595

Senum, S.R., Li, Y.S.M., Benson, K.A. et al. (25 more authors) (2022) Monoallelic IFT140 pathogenic variants are an important cause of the autosomal dominant polycystic kidney-spectrum phenotype. The American Journal of Human Genetics, 109 (1). pp. 136-156. ISSN 0002-9297