Items where Funder is LIFEARC.
APP49075 MR/Z506229/1
Mizielinska, S., Hautbergue, G.M. orcid.org/0000-0002-1621-261X, Gendron, T.F. et al. (5 more authors) (2025) Amyotrophic lateral sclerosis caused by hexanucleotide repeat expansions in C9orf72: from genetics to therapeutics. The Lancet Neurology, 24 (3). pp. 261-274. ISSN 1474-4422
BB/S005277/1
Mizielinska, S., Hautbergue, G.M. orcid.org/0000-0002-1621-261X, Gendron, T.F. et al. (5 more authors) (2025) Amyotrophic lateral sclerosis caused by hexanucleotide repeat expansions in C9orf72: from genetics to therapeutics. The Lancet Neurology, 24 (3). pp. 261-274. ISSN 1474-4422
Castelli, L.M., Lin, Y.-H., Sanchez-Martinez, A. et al. (19 more authors) (2023) A cell-penetrant peptide blocking C9ORF72-repeat RNA nuclear export reduces the neurotoxic effects of dipeptide repeat proteins. Science Translational Medicine, 15 (685). ISSN 1946-6234
IS-BRC-1215-20017
Mizielinska, S., Hautbergue, G.M. orcid.org/0000-0002-1621-261X, Gendron, T.F. et al. (5 more authors) (2025) Amyotrophic lateral sclerosis caused by hexanucleotide repeat expansions in C9orf72: from genetics to therapeutics. The Lancet Neurology, 24 (3). pp. 261-274. ISSN 1474-4422
MND005891
Castelli, L.M., Lin, Y.-H., Sanchez-Martinez, A. et al. (19 more authors) (2023) A cell-penetrant peptide blocking C9ORF72-repeat RNA nuclear export reduces the neurotoxic effects of dipeptide repeat proteins. Science Translational Medicine, 15 (685). ISSN 1946-6234
MR/R024162/1
Castelli, L.M., Lin, Y.-H., Sanchez-Martinez, A. et al. (19 more authors) (2023) A cell-penetrant peptide blocking C9ORF72-repeat RNA nuclear export reduces the neurotoxic effects of dipeptide repeat proteins. Science Translational Medicine, 15 (685). ISSN 1946-6234
MR/W00416X/1
Mizielinska, S., Hautbergue, G.M. orcid.org/0000-0002-1621-261X, Gendron, T.F. et al. (5 more authors) (2025) Amyotrophic lateral sclerosis caused by hexanucleotide repeat expansions in C9orf72: from genetics to therapeutics. The Lancet Neurology, 24 (3). pp. 261-274. ISSN 1474-4422