Systematic review of presymptomatic treatment for spinal muscular atrophy

Cooper, K. orcid.org/0000-0002-7702-8103, Nalbant, G. orcid.org/0000-0002-5414-9383, Sutton, A. orcid.org/0000-0003-2449-2516 et al. (5 more authors) (2024) Systematic review of presymptomatic treatment for spinal muscular atrophy. International Journal of Neonatal Screening, 10 (3). 56. ISSN 2409-515X

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Item Type: Article
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© 2024 by the authors. Licensee MDPI, Basel, Switzerland. This article is an open access article distributed under the terms and conditions of the Creative Commons Attribution (CC BY) license (https://creativecommons.org/licenses/by/4.0/).

Keywords: efficacy of treatment; presymptomatic treatment; spinal muscular atrophy; systematic review
Dates:
  • Published: September 2024
  • Published (online): 14 August 2024
  • Accepted: 29 July 2024
  • Submitted: 26 May 2024
Institution: The University of Sheffield
Academic Units: The University of Sheffield > Faculty of Medicine, Dentistry and Health (Sheffield) > School of Medicine and Population Health
Depositing User: Symplectic Sheffield
Date Deposited: 04 Sep 2024 10:47
Last Modified: 04 Sep 2024 10:47
Status: Published
Publisher: MDPI AG
Refereed: Yes
Identification Number: 10.3390/ijns10030056
Related URLs:
Sustainable Development Goals:
  • Sustainable Development Goals: Goal 3: Good Health and Well-Being
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