Items where authors include "Mendell, J.R."

Article

Meyer, K., Ferraiuolo, L., Schmelzer, L. et al. (11 more authors) (2014) Improving single injection CSF delivery of AAV9-mediated gene therapy for SMA: A dose-response study in mice and nonhuman primates. Molecular Therapy, 23 (3). 477 -487. ISSN 1525-0016