Translating SOD1 gene silencing towards the clinic: A highly efficacious, off-target free and biomarker-supported strategy for familial ALS

Iannitti, T., Scarrott, J., Likhite, S. et al. (12 more authors) (2018) Translating SOD1 gene silencing towards the clinic: A highly efficacious, off-target free and biomarker-supported strategy for familial ALS. Molecular Therapy : Nucleic Acids, 12. pp. 75-88. ISSN 2162-2531

Abstract

Metadata

Authors/Creators:
  • Iannitti, T.
  • Scarrott, J.
  • Likhite, S.
  • Coldicott, I.R.P.
  • Lewis, K.E.
  • Heath, P.R.
  • Higginbottom, A.
  • Myszczynska, M.A.
  • Milo, M.
  • Hautbergue, G.M.
  • Meyer, K.
  • Kaspar, B.K.
  • Ferraiuolo, L.
  • Shaw, P.J.
  • Azzouz, M. https://orcid.org/0000-0001-6564-5967
Copyright, Publisher and Additional Information: © 2018 The Author(s). This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/).
Dates:
  • Accepted: 28 April 2018
  • Published (online): 3 May 2018
  • Published: 7 September 2018
Institution: The University of Sheffield
Academic Units: The University of Sheffield > Sheffield Teaching Hospitals
Funding Information:
FunderGrant number
EUROPEAN RESEARCH COUNCILGTNCTV - 294745
MEDICAL RESEARCH COUNCILG1001492/1
Depositing User: Symplectic Sheffield
Date Deposited: 04 May 2018 11:49
Last Modified: 01 Nov 2018 12:11
Published Version: https://doi.org/10.1016/j.omtn.2018.04.015
Status: Published
Publisher: Nature Publishing Group
Refereed: Yes
Identification Number: https://doi.org/10.1016/j.omtn.2018.04.015

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