Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy

Powis, R.A, Karyka, E., Boyd, P. et al. (13 more authors) (2016) Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy. JCI Insight, 1 (11). e87908. ISSN 2379-3708

Abstract

Metadata

Authors/Creators:
  • Powis, R.A
  • Karyka, E.
  • Boyd, P.
  • Come, J.
  • Jones, R.A.
  • Zheng, Y.
  • Szunyogova, E.
  • Groen, E.J.N.
  • Hunter, G.
  • Thomson, D.
  • Wishart, T.M.
  • Becker, C.G.
  • Parson, S.H.
  • Martinat, S.
  • Azzouz, M.
  • Gillingwater, T.H.
Copyright, Publisher and Additional Information: © 2016 American Society for Clinical Investigation
Dates:
  • Published (online): 21 July 2016
  • Accepted: 16 June 2016
  • Published: 2016
Institution: The University of Sheffield
Academic Units: The University of Sheffield > Faculty of Medicine, Dentistry and Health (Sheffield) > Department of Neuroscience (Sheffield)
The University of Sheffield > Sheffield Teaching Hospitals
Depositing User: Symplectic Sheffield
Date Deposited: 25 Jul 2016 15:45
Last Modified: 18 Jul 2017 11:04
Published Version: http://dx.doi.org/10.1172/jci.insight.87908
Status: Published
Publisher: The American Society for Clinical Investigation
Refereed: Yes
Identification Number: https://doi.org/10.1172/jci.insight.87908

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